[Kalydeco helps about 4 percent of the people with a certain mutation of cystic fibrosis, and the drug probably will be useful for 16 percent of CF patients over the next couple of years, said Dr. Robert Beall, president and CEO of the Cystic Fibrosis Foundation. Trials are under way that combine Kalydeco and another drug to see if the combination could help the majority of those with CF, he said.]
[The effectiveness is good news for Stephanie Dudley of Shenandoah, Iowa. Zach, her son, was asked to take part in the clinical trial 2½ years ago. In the two years he has been on the pills, she said, he has grown 10 inches, gained 20 to 30 pounds and "his breathing tests have just shot through the roof," she said.]
Thirdme, Thanks for pointing this out. I'm constantly trolling now-a-days to get me through the next four years and that story is not just typical, but understates what this drug is doing. Weight gain/growth, old mucus plugs cleared, SC dropping amazing levels, aquagenic wrinkling gone, coughing gone, treatments being scaled back substantially. Just imagine what 661/Kalydeco could do if it is working on both mutations!!
I appreciate your contribution to the intellectual properties of this board. You have eye-opening insights into the medicine and science of CF. I am sure that readers of your messages will benefit a lot.