"yeah at 234K euros for a year supply. why so expensive? the molecule isn't that outrageous. wonder how many steps to make it? "
Drug pricing is not based on the cost of production. It is based on the cost of researching/developing the drug from pre-clinical stage though phase III, the marketing cost, and most important, the size of the population it will serve -- the smaller the size, the higher the cost and that is the reason also for drug orphan designation.