I've been involved for a few years off and on. Mostly off until this year. I have a family member with DMD and understand what we're up against. I've done fund raising for PPMD, donated money to PPMD and have been to the conferences. I'm no expert for sure, and no doubt, you know more about this company than I do. Just hoping eteplirsen is the real deal. I get a kick out of your perspective sometimes. I enjoy your posts and appreciate your sincerity.
I believe we'll get AA because we're losing this fight to DMD and it ain't even close. I've seen firsthand what DMD does up to age 16 to a boy that I love. I know how the story goes from here without intervention. It's a cruel and ruthless disease and eteplirsen is a miracle so far. Availability must be accelerated to all so we can find out how powerful it is over time. My best to you.