CBS NEWS: Families Driving to Washington This Weekend, Asking For Approval Now.
Beverly Family To Plead With FDA To Approve Drug
February 6, 2013 11:44 PM
Reporting Jonathan Elias
BEVERLY (CBS) – A Massachusetts family is in a fight to save their son.
They’re going to Washington to plead with the FDA to approve a drug that would give them some hope.
There is no cure, but for the last two years, a drug in the testing phase has shown signs of progress.
The Gaudenzis are traveling to D.C. this weekend to try and convince lawmakers and the FDA to release the drug now. The drug being tested is Eteplirsen.
“My fear is that our boys at this age will be too disabled or even alive to benefit from this drug,” said Natalie.
This form of muscular dystrophy affects mostly boys. Many of them will join the Gaudenzis in Washington to persuade the FDA to put the drug’s approval on the fast track.