search "billy ellsworth sarepta video"
this was a video of one of the srpt trial boys from pittsburgh
last fall he was improving but continued to be a dmd "toe walker"
we now know, after the ppmd conference, that he is no longer a toe walker
that seems to be a significant every day life improvement to me
And............. He has his HEALTHY kidneys intact too! Heck, I bet he doesn't bleed for two hours when he falls and scrapes his elbow either. No longer toe walking is a remarkable improvement.