Please reply to this message with the % probability that SRPT will get Accelerated Approval by the FDA?
My vote is 55% chance they will get it, so just over 50-50.
I'm going with 25%. I am long and hope I am wrong - especially for the kids - but not expecting it at this point. Think the drug works and will save a lot of lives. So I really hope I am wrong. Either way I am buying more after we find out whether AA or not. Barring AA and a stock price over $75, I am planning on adding more post-news of the timeline for approval.
There's a lot of people in the same camp as you. The drug works but the FDA won't approve it yet. Think about this for a minute. If the FDA feels the same way (which I believe they will), the new regulations make it much easier to approve a drug that everyone know works well. We don't need Phase 3 trials and hundreds of patients in a trial for approval if you know the drug worksh. The FDA would be doing the public a huge disservice if they knew a drug worked and they didn't approve it because it didn't fit in a nice box of a large Phase 3 trial.