This is the first report to document, in animal models, new [disease-causing] gene mutations for Alzheimer's since the reports of the original four genes in the 1990s," study senior author Rudolph Tanzi, director of the genetics and aging unit at the MassGeneral Institute for Neurodegenerative Disease, said in a hospital news release.
During the review process, the TGA requirements for data follow those for the European Union; however, they will accept US dossiers (by prior agreement) for high priority drugs (eg, drugs to treat cancers).
Srpt is a one trick pony! As Duchenne MD is a rare disease! I hope they get it rite.
Srpt and pran have nothing in common.