RARE - Ultragenyx Pharmaceutical Inc.

NasdaqGS - NasdaqGS Real Time Price. Currency in USD
57.46
-1.00 (-1.71%)
As of 2:42PM EST. Market open.
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Previous Close58.46
Open58.43
Bid57.42 x 1000
Ask57.51 x 1400
Day's Range56.91 - 58.50
52 Week Range35.41 - 74.50
Volume288,062
Avg. Volume577,374
Market Cap3.32B
Beta (5Y Monthly)2.14
PE Ratio (TTM)N/A
EPS (TTM)-7.24
Earnings DateFeb 16, 2020 - Feb 20, 2020
Forward Dividend & YieldN/A (N/A)
Ex-Dividend DateN/A
1y Target Est70.95
  • Benzinga

    The Daily Biotech Pulse: Osmotica Soars On Insider Buys, Ultragenyx's Partnered Rare Disease Drug Moves Into Clinics

    Here's a roundup of top developments in the biotech space over the last 24 hours. Scaling The Peaks (Biotech Stocks Hitting 52-week highs on Jan. 15) 10X Genomics Inc (NASDAQ: TXG ) Aimmune Therapeutics ...

  • GlobeNewswire

    GeneTx and Ultragenyx Announce Investigational New Drug (IND) Application Active for GTX-102 in Patients with Angelman Syndrome

    GeneTx Biotherapeutics LLC and Ultragenyx Pharmaceutical Inc. (RARE), a biopharmaceutical company focused on the development of novel products for serious rare and ultra-rare diseases, today announced that GeneTx’s Investigational New Drug (IND) Application for GTX-102, an experimental antisense oligonucleotide being evaluated for the treatment of Angelman syndrome (AS), filed with the U.S. Food and Drug Administration (FDA) is now active. "The FDA’s clearance of the IND to evaluate GTX-102 in patients with Angelman syndrome represents a significant milestone for the Angelman community,” said Paula Evans, Chief Executive Officer at GeneTx.

  • Ultragenyx Provides Preliminary Crysvita 2019 Revenues
    Zacks

    Ultragenyx Provides Preliminary Crysvita 2019 Revenues

    Ultragenyx (RARE) provides preliminary 2019 revenue numbers and 2020 outlook for Crysvita, along with other pipeline updates.

  • Ultragenyx's Gene Therapy Positive in Genetic Disorder Study
    Zacks

    Ultragenyx's Gene Therapy Positive in Genetic Disorder Study

    Shares of Ultragenyx (RARE) rise 23.4% after releasing positive top-line data from the phase I/II study of its gene therapy candidate DTX301 for the treatment of OTC deficiency.

  • GlobeNewswire

    Ultragenyx Reports Preliminary 2019 Revenue and Provides 2020 Crysvita Revenue Guidance

    Ultragenyx Pharmaceutical Inc. (RARE), a biopharmaceutical company focused on the development of novel products for serious rare and ultra-rare genetic diseases, today reported preliminary unaudited 2019 revenue and cash and investments at year end 2019, and provided 2020 revenue guidance for Crysvita in Ultragenyx territories.

  • GlobeNewswire

    Ultragenyx and Kyowa Kirin Announce Submission of Supplemental Biologics License Application to U.S. FDA for Crysvita® (burosumab) for Tumor-Induced Osteomalacia (TIO)

    Ultragenyx Pharmaceutical Inc. (RARE), a biopharmaceutical company focused on the development of novel products for rare and ultra-rare diseases, and Kyowa Kirin Co., Ltd., (Kyowa Kirin, TYO: 4151) today announced that they submitted a supplemental Biologics License Application (sBLA) to the U.S. Food and Drug Administration (FDA) on December 18, 2019, for Crysvita® (burosumab) for the treatment of FGF23-related hypophosphatemia associated with phosphaturic mesenchymal tumors (tumor-induced osteomalacia; TIO) that cannot be curatively resected or localized. The companies expect to hear back from FDA on submission acceptance and review designation in February 2020. “Approximately half of patients with TIO have tumors that cannot be surgically removed, leaving them with no other current treatment options,” said Camille L. Bedrosian, M.D., Chief Medical Officer of Ultragenyx.

  • Benzinga

    The Daily Biotech Pulse: Positive Data Readouts To Spur Aclaris, Moderna And Ultragenyx

    Here's a roundup of top developments in the biotech space over the last 24 hours. Scaling The Peaks (Biotech Stocks Hitting 52-week highs on Jan. 9) Acceleron Pharma Inc (NASDAQ: XLRN ) Allergan plc (NYSE: ...

  • GlobeNewswire

    Ultragenyx Announces Positive Topline Cohort 3 Results and Improved Longer-Term Cohort 2 Results from Phase 1/2 Study of DTX301 Gene Therapy in Ornithine Transcarbamylase (OTC) Deficiency

    Ultragenyx Pharmaceutical Inc. (RARE), a biopharmaceutical company focused on the development of novel products for rare and ultra-rare diseases, today announced topline positive safety and efficacy data from Cohort 3 and longer-term data from Cohort 2 of the ongoing Phase 1/2 study of DTX301, an investigational adeno-associated virus (AAV) gene therapy for the treatment of ornithine transcarbamylase (OTC) deficiency. In Cohort 3 (n=3), there were two confirmed female responders as well a third potential male responder who requires longer-term follow-up to confirm response status.

  • Benzinga

    Week Ahead In Biotech: PDUFA Date Ahead For Astra Zeneca, Merck's Lynparza, Pending Clinical Readouts In Focus

    Biotech stocks advanced in the penultimate week of the year, and the iShares NASDAQ Biotechnology Index (NASDAQ: IBB ) is on track to end the year with gains in excess of 25%. The previous week saw FDA ...

  • GlobeNewswire

    Ultragenyx to Present at 38ᵗʰ Annual J.P. Morgan Healthcare Conference

    Ultragenyx Pharmaceutical Inc. (RARE), a biopharmaceutical company focused on the development of novel products for serious rare and ultra-rare genetic diseases, today announced that Emil D. Kakkis, M.D., Ph.D., the company's Chief Executive Officer and President, will present at the 38th Annual J.P. Morgan Healthcare Conference on Tuesday, January 14, 2020 at 12:00 pm PT in San Francisco. The live and archived webcast of the presentation will be accessible from the company’s website at http://ir.ultragenyx.com/events.cfm. Ultragenyx is a biopharmaceutical company committed to bringing patients novel products for the treatment of serious rare and ultra-rare genetic diseases.

  • GlobeNewswire

    Ultragenyx Announces Sale of Future European Royalties on Crysvita® (burosumab) for $320 Million to Royalty Pharma

    Ultragenyx Pharmaceutical Inc. (RARE), a biopharmaceutical company focused on the development of novel products for rare and ultra-rare diseases, and Royalty Pharma today announced that Ultragenyx has sold to Royalty Pharma for $320 million a royalty right due to Ultragenyx from Kyowa Kirin Co., Ltd for the net sales of Crysvita® (burosumab) in the European Union (EU), the United Kingdom (UK), and Switzerland. Crysvita has received conditional marketing authorization in Europe for the treatment of X-linked hypophosphatemia (XLH) with radiographic evidence of bone disease in children 1 year of age and older and adolescents with growing skeletons, and an application for the expanded use in adults with XLH is currently under review by the European Medicines Agency.

  • Do Hedge Funds Love Ultragenyx Pharmaceutical Inc (RARE)?
    Insider Monkey

    Do Hedge Funds Love Ultragenyx Pharmaceutical Inc (RARE)?

    We are still in an overall bull market and many stocks that smart money investors were piling into surged through the end of November. Among them, Facebook and Microsoft ranked among the top 3 picks and these stocks gained 54% and 51% respectively. Hedge funds' top 3 stock picks returned 41.7% this year and beat […]

  • GuruFocus.com

    Astellas-Audentes Deal Likely to Ignite More Acquisitions

    Companies with gene therapy capabilities are becoming more attractive to members of Big Pharma, who are eager to add the technology to their portfolios Continue reading...

  • Ultragenyx (RARE) Up 13.6% Since Last Earnings Report: Can It Continue?
    Zacks

    Ultragenyx (RARE) Up 13.6% Since Last Earnings Report: Can It Continue?

    Ultragenyx (RARE) reported earnings 30 days ago. What's next for the stock? We take a look at earnings estimates for some clues.

  • Companies Like Ultragenyx Pharmaceutical (NASDAQ:RARE) Are In A Position To Invest In Growth
    Simply Wall St.

    Companies Like Ultragenyx Pharmaceutical (NASDAQ:RARE) Are In A Position To Invest In Growth

    Just because a business does not make any money, does not mean that the stock will go down. For example, although...

  • GlobeNewswire

    Ultragenyx to Present at Piper Jaffray 31st Annual Healthcare Conference

    Ultragenyx Pharmaceutical Inc. (RARE), a biopharmaceutical company focused on the development of novel products for serious rare and ultra-rare genetic diseases, today announced that Shalini Sharp, the company’s Chief Financial Officer, will present at the Piper Jaffray 31st Annual Healthcare Conference on Wednesday, December 4, 2019 at 2:00 PM ET in New York, NY. The live and archived webcast of the presentation will be accessible from the company’s website at http://ir.ultragenyx.com/events.cfm. Ultragenyx is a biopharmaceutical company committed to bringing patients novel products for the treatment of serious rare and ultra-rare genetic diseases.

  • Thomson Reuters StreetEvents

    Edited Transcript of RARE earnings conference call or presentation 5-Nov-19 10:00pm GMT

    Q3 2019 Ultragenyx Pharmaceutical Inc Earnings Call

  • After son’s rare disease diagnosis, father finds hope through film festival
    American City Business Journals

    After son’s rare disease diagnosis, father finds hope through film festival

    A Mission Bay film festival this weekend is aimed at filmmakers and film lovers, but more so at patients, advocates, doctors and researchers dealing with rare diseases.

  • GlobeNewswire

    Ultragenyx to Present at Upcoming Investor Conferences

    Emil D. Kakkis, M.D., Ph.D., the company's Chief Executive Officer and President, will present at the Credit Suisse 28th Annual Healthcare Conference on Tuesday, November 12, 2019 at 11:30 AM MT in Scottsdale, Arizona. Tom Kassberg, the company’s Chief Business Officer, will present at the Stifel Healthcare Conference on Wednesday, November 20, 2019 at 1:50 PM ET in New York, NY. The live and archived webcast of the company presentations will be accessible from the company’s website at http://ir.ultragenyx.com/events.cfm.

  • Ultragenyx (RARE) Reports Wider-Than-Expected Loss in Q3
    Zacks

    Ultragenyx (RARE) Reports Wider-Than-Expected Loss in Q3

    Ultragenyx (RARE) reports wider-than-expected loss and misses sales estimates in the third quarter of 2019.

  • Ultragenyx (RARE) Reports Q3 Loss, Lags Revenue Estimates
    Zacks

    Ultragenyx (RARE) Reports Q3 Loss, Lags Revenue Estimates

    Ultragenyx (RARE) delivered earnings and revenue surprises of -14.62% and -9.80%, respectively, for the quarter ended September 2019. Do the numbers hold clues to what lies ahead for the stock?

  • GlobeNewswire

    Ultragenyx Reports Third Quarter 2019 Financial Results and Corporate Update

    Strong Crysvita® (burosumab) Launch Continues with Approximately 1,130 Patients on Reimbursed Commercial Therapy in the United States as of the end of the Third Quarter UX007.

  • GlobeNewswire

    Ultragenyx to Host Conference Call for Third Quarter 2019 Financial Results and Corporate Update

    Ultragenyx Pharmaceutical Inc. (RARE), a biopharmaceutical company focused on the development of novel products for serious rare and ultra-rare genetic diseases, today announced that it will host a conference call on Tuesday, November 5, 2019 at 5pm ET to discuss third quarter 2019 financial results and provide a corporate update. Ultragenyx is a biopharmaceutical company committed to bringing to patients novel products for the treatment of serious rare and ultra-rare genetic diseases. The company has built a diverse portfolio of approved therapies and product candidates aimed at addressing diseases with high unmet medical need and clear biology for treatment, for which there are typically no approved therapies treating the underlying disease.

  • Ultragenyx (RARE) Expected to Beat Earnings Estimates: Should You Buy?
    Zacks

    Ultragenyx (RARE) Expected to Beat Earnings Estimates: Should You Buy?

    Ultragenyx (RARE) possesses the right combination of the two key ingredients for a likely earnings beat in its upcoming report. Get prepared with the key expectations.

  • Were Hedge Funds Right About Dumping Ultragenyx Pharmaceutical Inc (RARE)?
    Insider Monkey

    Were Hedge Funds Right About Dumping Ultragenyx Pharmaceutical Inc (RARE)?

    "Since 2006, value stocks (IVE vs IVW) have underperformed 11 of the 13 calendar years and when they beat growth, it wasn't by much. Cumulatively, through this week, it has been a 122% differential (up 52% for value vs up 174% for growth). This appears to be the longest and most severe drought for value […]